{"identifier":"nobleid:/w1/20260526/4C700D1E","arkIdentifier":"ark:/48914/w1/20260526/4C700D1E","version":1,"workTitle":"Phase 2a Study of Ataluren-Mediated Dystrophin Production in Patients with Nonsense Mutation Duchenne Muscular Dystrophy","workType":"Journal Article","authors":"Richard S. Finkel, Kevin M. Flanigan, Brenda Wong, Carsten Bönnemann, Jacinda Sampson, H. Lee Sweeney, Allen Reha, Valerie J. Northcutt, Gary Elfring, Jay Barth","description":null,"workUrl":null,"createdAt":"2026-05-26T04:02:16.852345Z","canonicalUrl":"https://nobleid.org/ark:/48914/w1/20260526/4C700D1E.v1"}