Optimized genomic editing of a common Duchenne muscular dystrophy mutation in patient-derived muscle cells and a new humanized mouse model

Mateusz Z. Durbacz; Yu Zhang; Hui Li; Takahiko Nishiyama; Efrain Sanchez- Ortiz; John R. McAnally; Damir Alzhanov; Ning Liu; Eric N. Olson

doi:https://doi.org/10.1016/j.omtn.2025.102569

Optimized genomic editing of a common Duchenne muscular dystrophy mutation in patient-derived muscle cells and a new humanized mouse model

Identifier:nobleid.org/w1/20260418/58AB1E7D

Type:Journal Article

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Efrain Sanchez- Ortiz

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Optimized genomic editing of a common Duchenne muscular dystrophy mutation in patient-derived muscle cells and a new humanized mouse model

Identifier:nobleid.org/w1/20260418/58AB1E7D

Type:Journal Article

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